Spinraza:

Spinraza is a drug indicated for the treatment of a genetic disease called spinal muscular atrophy, because it contains some of the genetic material capable of causing the production by the SMN-2 gene of a protein normally produced by the SMN-1 gene, a substance missing in cases of spinal muscular atrophy. This reduces neuron loss […]

Spinraza is a medicine that causes the SMN-2 gene to produce a protein that is normally produced by the SMN-1 gene, replacing it. Therefore, this medicine is used to treat cases of spinal muscular atrophy, which develops due to the absence or defect of the SMN-1 gene in the body. Although this drug has already